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Limb-girdle Muscular Dystrophy Type 2A - 11 Studies Found
Status | Study |
Recruiting |
Study Name: rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies Condition: Dysferlinopathy Date: 2016-02-11 Interventions: Drug: rAAVrh74.MHCK7.DYSF.DV Biological/Vaccine: rAAVrh74.MHCK7.DYSF.DV Recombinant adeno-associated vir |